A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.

For the second time, a person with DMD has died of acute liver failure after being treated with the one-time gene therapy Elevidys.

Patients are often the best experts on their disease, but what about emergency situations? Columnist Patrick Moeschen shares ...

The U.S. Food and Drug Administration (FDA) granted platform technology designation to the viral vector used in SRP-9003, an ...

As a Duchenne muscular dystrophy survivor, I’ve spent much of my life on the outside looking in, especially when it comes to public events like concerts and sporting events. My condition affects not ...

Columnist Robin Stemple marks two anniversaries that forever altered his life. Despite the incredible challenges, he feels ...

The one-time gene therapy Elevidys (delandistrogene moxeparvovec-rokl) was associated with stabilizations in motor function for boys with Duchenne muscular dystrophy (DMD) who were treated when they ...

As her only son without DMD plays in a statewide all-star football game, columnist Betty Vertin reflects on his tie to his brothers.

An investigational gene therapy called GNT0004 has demonstrated sustained stabilization of motor function at up to two years of follow-up in two boys with Duchenne muscular dystrophy (DMD). The boys ...

If you’ve read any of my recent columns, you know that I’ve had a lot of health struggles of late. I’m back on the medical merry-go-round with physical therapy, occupational therapy, medical ...

Note: This story was updated May 19, 2025, to clarify the requirements needed for Elevidys to transition to full approval. The Japanese Ministry of Health, Labour, and Welfare (MHLW) has conditionally ...