Duchenne muscular dystrophy families are sharing stories about Elevidys complications on social media. But they aren’t ...

Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne), will host its 2025 Annual Conference in Las Vegas, Nevada, June ...

In this week’s edition of InnovationRx, we look at the dangers of RFK Jr.’s vaccine advisory committee, how Trump’s visa ban ...

In another tragic incident, Sarepta Therapeutics (NASDAQ: SRPT) saw a second death in connection with its Duchenne muscular ...

I am upgrading Dyne Therapeutics stock to a 'Buy' rating due to promising late-stage DM1 and DMD drug candidates and ...

A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.

Many parents said they were afraid of noninvasive ventilation, with some citing inaccurate concerns about ventilation devices.

"There were tears everywhere," Hana Herrick, school services coordinator at Lurie Children’s Hospital, tells PEOPLE ...